[{"data":1,"prerenderedAt":-1},["ShallowReactive",2],{"health-study-detail:100610743":3},{"organization":4,"armGroups":7,"interventions":10,"overallOfficials":11,"centralContacts":43,"locations":49,"responsibleParty":62,"collaborators":10,"id":64,"slug":65,"hasResults":66,"nctId":67,"briefTitle":68,"officialTitle":68,"acronym":69,"eligibilityCriteria":70,"healthyVolunteers":66,"sex":71,"minAge":10,"maxAge":10,"enrollmentInfo":72,"targetDuration":10,"studyType":75,"phases":10,"briefSummary":76,"conditions":77,"keywords":79,"overallStatus":52,"whyStopped":10,"lastUpdateSubmitDate":84,"lastUpdatePostDateStruct":85,"startDateStruct":88,"completionDateStruct":90,"leadSponsor":92,"locationsCount":93},{"fullName":5,"class":6},"Fundació Sant Joan de Déu","OTHER",[8],{"label":9,"type":10,"description":9,"interventionNames":10},"Subjects with Spinal Muscular Atrophy 5q",null,[12,16,19,22,25,28,30,33,36,39,41],{"name":13,"affiliation":14,"role":15},"Andrés Nascimento","Hospital Sant Joan de Deu","STUDY_CHAIR",{"name":17,"affiliation":18,"role":15},"Mónica Povedano Panadés","Hospital Universitari de Bellvitge",{"name":20,"affiliation":21,"role":15},"Francina Munell Casadesús","Hospital Universitari Vall d'Hebrón",{"name":23,"affiliation":24,"role":15},"Miguel Angel Fernández García Miguel Angel Fernández García","Hospital Universitario La Paz",{"name":26,"affiliation":27,"role":15},"Inmaculada Pitarch Castellano","Hospital Universitario La Fe",{"name":29,"affiliation":27,"role":15},"Juan Francisco Vázquez Costa",{"name":31,"affiliation":32,"role":15},"Maria Grazia Cattinari","Fundación Atrofia Muscular Espinal",{"name":34,"affiliation":35,"role":15},"Rocío Calvo","Hospital Universitario Regional de Málaga",{"name":37,"affiliation":38,"role":15},"Eduardo Martínez Salcedo","Hospital Universitario Virgen de la Arrixaca",{"name":40,"affiliation":38,"role":15},"Antonio Moreno Escribano",{"name":42,"affiliation":14,"role":15},"Julita Medina Cantillo",[44],{"name":45,"role":46,"phone":47,"phoneExt":10,"email":48},"CUIDAME Project Manager","CONTACT","0034 936 009 751","info@registro-cuidame.org",[50],{"facility":51,"status":52,"city":53,"state":10,"zip":10,"country":54,"countryCode":55,"cosmosGeoPoint":56,"geoPoint":61,"contacts":10},"Hospital Sant Joan de Déu","RECRUITING","Esplugues de Llobregat","Spain","ES",{"type":57,"coordinates":58},"Point",[59,60],2.08809,41.37732,{"lat":60,"lon":59},{"type":63,"investigatorFullName":10,"investigatorTitle":10,"investigatorAffiliation":10,"oldNameTitle":10,"oldOrganization":10},"SPONSOR","100610743","cuidame-longitudinal-data-collection-from-patients-with-spinal-muscular-atrophy-in-spain-100610743",false,"NCT07231549","CuidAME: Longitudinal Data Collection From Patients With Spinal Muscular Atrophy in Spain","CUIDAME","Inclusion Criteria:\n\n* Genetically confirmed 5q SMA\n* Patient or caregivers written informed consent has been obtained (except for paediatric patients deceased).\n\nExclusion Criteria:\n\n* Further types of SMA (non-5q SMA).\n* Patient without legal capacity who cannot understand the nature, significance, and consequences of the project.","ALL",{"count":73,"type":74},1000,"ESTIMATED","OBSERVATIONAL","The goal of this observational study is to set up a longitudinal data collection study to perform a long-term follow-up of SMA patients in a real-world setting, and to standardise and homogenize the data collection process for SMA patient's data.\n\nTreated and untreated patients will be followed based on the routine clinical practice schedule.",[78],"Spinal Muscular Atrophy",[80,81,82,83],"registry","natural history","adult","pediatric","2025-11-14",{"date":86,"type":87},"2025-11-17","ACTUAL",{"date":89,"type":87},"2020-05-05",{"date":91,"type":74},"2026-12",{"name":5,"class":6},1]