[{"data":1,"prerenderedAt":-1},["ShallowReactive",2],{"health-study-detail:100497300":3},{"organization":4,"armGroups":7,"interventions":7,"overallOfficials":8,"centralContacts":13,"locations":24,"responsibleParty":81,"collaborators":83,"id":92,"slug":93,"hasResults":94,"nctId":95,"briefTitle":96,"officialTitle":97,"acronym":98,"eligibilityCriteria":99,"healthyVolunteers":94,"sex":100,"minAge":7,"maxAge":7,"enrollmentInfo":101,"targetDuration":104,"studyType":105,"phases":7,"briefSummary":106,"conditions":107,"keywords":109,"overallStatus":27,"whyStopped":7,"lastUpdateSubmitDate":112,"lastUpdatePostDateStruct":113,"startDateStruct":116,"completionDateStruct":118,"leadSponsor":120,"locationsCount":121},{"fullName":5,"class":6},"Fondazione Policlinico Universitario Agostino Gemelli IRCCS","OTHER",null,[9],{"name":10,"affiliation":11,"role":12},"Eugenio Mercuri, MD","F Policlinico Gemelli IRCCS","PRINCIPAL_INVESTIGATOR",[14,19],{"name":10,"role":15,"phone":16,"phoneExt":17,"email":18},"CONTACT","06 3015","5340","eugeniomaria.mercuri@policlinicogemelli.it",{"name":20,"role":15,"phone":21,"phoneExt":22,"email":23},"Marika Pane, MD","063015","6742","marika.pane@policlinicogemelli.it",[25,40,51,62,73],{"facility":26,"status":27,"city":28,"state":7,"zip":7,"country":29,"countryCode":30,"cosmosGeoPoint":31,"geoPoint":36,"contacts":37},"Istituto Gaslini","RECRUITING","Genova","Italy","IT",{"type":32,"coordinates":33},"Point",[34,35],11.87211,45.21604,{"lat":35,"lon":34},[38],{"name":39,"role":15,"phone":7,"phoneExt":7,"email":7},"Claudio Bruno",{"facility":41,"status":27,"city":42,"state":7,"zip":7,"country":29,"countryCode":30,"cosmosGeoPoint":43,"geoPoint":47,"contacts":48},"Nemo Sud","Messina",{"type":32,"coordinates":44},[45,46],15.55256,38.19394,{"lat":46,"lon":45},[49],{"name":50,"role":15,"phone":7,"phoneExt":7,"email":7},"Sonia Messina",{"facility":52,"status":27,"city":53,"state":7,"zip":7,"country":29,"countryCode":30,"cosmosGeoPoint":54,"geoPoint":58,"contacts":59},"Centro Clinico nemo","Milan",{"type":32,"coordinates":55},[56,57],12.59836,42.78235,{"lat":57,"lon":56},[60],{"name":61,"role":15,"phone":7,"phoneExt":7,"email":7},"Valeria Sansone",{"facility":63,"status":27,"city":64,"state":7,"zip":7,"country":29,"countryCode":30,"cosmosGeoPoint":65,"geoPoint":69,"contacts":70},"Ospedale Bambino gesu","Rome",{"type":32,"coordinates":66},[67,68],12.51133,41.89193,{"lat":68,"lon":67},[71],{"name":72,"role":15,"phone":7,"phoneExt":7,"email":7},"Adele D'Amico",{"facility":74,"status":27,"city":64,"state":7,"zip":7,"country":29,"countryCode":30,"cosmosGeoPoint":75,"geoPoint":77,"contacts":78},"Policlinico gemelli",{"type":32,"coordinates":76},[67,68],{"lat":68,"lon":67},[79],{"name":80,"role":15,"phone":21,"phoneExt":17,"email":18},"Eugenio Mercuri",{"type":82,"investigatorFullName":7,"investigatorTitle":7,"investigatorAffiliation":7,"oldNameTitle":7,"oldOrganization":7},"SPONSOR",[84,86,88,90],{"name":85,"class":6},"University of Milan",{"name":87,"class":6},"Istituto Giannina Gaslini",{"name":89,"class":6},"Ospedale Pediatrico Bambin Gesù",{"name":91,"class":6},"University of Messina","100497300","natural-history-of-sma-100497300",false,"NCT05755451","Natural History of SMA","Natural History of SMA: Long Term Longitudinal Study and Development of a Registry","iSMAR","Inclusion Criteria:\n\nall patients\n\nExclusion Criteria:\n\nif enrolled in clinical trials","ALL",{"count":102,"type":103},1200,"ESTIMATED","15 Years","OBSERVATIONAL","This is an investigator initiated observational study with the aim to record several aspects of function, care and adverse events in a large cohort of SMA patients followed longitudinally by using a structured academic disease registry.",[108],"Muscular Atrophy, Spinal",[110,111],"natural history","spinal muscular atrophy","2023-03-02",{"date":114,"type":115},"2023-03-06","ACTUAL",{"date":117,"type":115},"2018-06-21",{"date":119,"type":103},"2033-12-30",{"name":5,"class":6},5]