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We will also learn about how this condition impacts other body systems.\n\nParticipants will undergo:\n\n* Neuromuscular assessments\n* Blood collections\n* Swallowing and breathing assessments\n* Questionnaires",[301],"LAMA2-MD \\(Merosin Deficient Congenital Muscular Dystrophy, MDC1A\\)",[303,304,305,306,307],"Early Phase 1","Observational","Natural History","Neuromuscular","Functional Assessments","2026-04-06",{"date":310,"type":311},"2026-04-08","ACTUAL",{"date":313,"type":311},"2025-05-12",{"date":315,"type":297},"2028-09",{"name":5,"class":6},14]