[{"data":1,"prerenderedAt":-1},["ShallowReactive",2],{"health-studies-list:{\"conditionNormalized\":\"cholesterol-ester-storage-disease\",\"overallStatus\":[\"RECRUITING\",\"AVAILABLE\",\"NOT_YET_RECRUITING\"],\"orderBy\":\"LastUpdateSubmitDate:desc\",\"size\":25,\"offset\":0}":3,"health-study-condition:cholesterol-ester-storage-disease":26},{"pageToken":4,"total":5,"offset":6,"count":5,"results":7},null,1,0,[8],{"id":9,"slug":10,"hasResults":11,"nctId":12,"briefTitle":13,"officialTitle":14,"acronym":15,"eligibilityCriteria":16,"healthyVolunteers":11,"sex":17,"minAge":4,"maxAge":4,"enrollmentInfo":18,"targetDuration":21,"studyType":22,"phases":4,"briefSummary":23,"conditions":24,"keywords":4,"overallStatus":32,"whyStopped":4,"lastUpdateSubmitDate":33,"lastUpdatePostDateStruct":34,"startDateStruct":37,"completionDateStruct":39,"leadSponsor":41,"locationsCount":44},"100181221","lysosomal-acid-lipase-lal-deficiency-registry-100181221",false,"NCT01633489","Lysosomal Acid Lipase (LAL) Deficiency Registry","An Observational Disease and Clinical Outcomes Registry of Patients With Lysosomal Acid Lipase (LAL) Deficiency","ALX-LALD-501","Patients must have a confirmed diagnosis of LAL Deficiency. An Informed Consent and Authorization must be obtained prior to patient enrollment where required under applicable laws and regulations, or a waiver must be obtained by the Institutional Review Board\u002FIndependent Ethics Committee.\n\nPatients cannot be currently participating in an Alexion-sponsored clinical trial. Patients who have concluded participation in an Alexion-sponsored sebelipase alfa clinical trial are eligible to enroll in this Registry, and enrollment in the Registry will not exclude a patient from enrolling in a future clinical trial.","ALL",{"count":19,"type":20},300,"ESTIMATED","10 Years","OBSERVATIONAL","This is an observational, multi-center, international disease registry designed to collect longitudinal data and create a knowledge base that will be utilized to improve the care and treatment of patients with LAL Deficiency. Participation in the Registry by both physicians and patients is voluntary.",[25,26,27,28,29,30,31],"Lysosomal Acid Lipase Deficiency","Cholesterol Ester Storage Disease","Wolman Disease","Acid Cholesteryl Ester Hydrolase Deficiency, Type 2","Acid Lipase Deficiency","LIPA Deficiency","LAL-Deficiency","RECRUITING","2026-03-04",{"date":35,"type":36},"2026-03-06","ACTUAL",{"date":38,"type":36},"2013-05-30",{"date":40,"type":20},"2029-08-30",{"name":42,"class":43},"Alexion Pharmaceuticals, Inc.","INDUSTRY",104]