Disease Progression in Women With X-linked Adrenoleukodystrophy
ConditionX-linked Adrenoleukodystrophy
Trial statusRecruiting
Trial phaseNot listed
Trial typeObservational
Biological sexFemale
Age18+
SponsorMinoryx Therapeutics, S.L.
About this trial
Observational, single-site prospective and minimally interventional study in women with X-linked adrenoleukodystrophy (ALD), conducted in France.
Eligibility criteria
Qualifiers
Women aged 18 years old or older.
Diagnosis of X-linked ALD based on genetic testing, altered VLCFA levels, or family history.
Willing to undergo annual follow-up visits, including brain and spinal cord MRI scans.
Provision of written informed consent.
Disqualifiers
Any condition that in the opinion of the investigator are likely to adversely affect the study participation, interfere with study compliance, or confound the study results.
Under treatment or previous treatment with leriglitazone.
Pregnant or lactating women.
Subjects benefiting from laws aimed at protecting vulnerable adults: subjects being deprived of liberty by judicial or administrative decision, subjects under guardianship.
Trial design
Treatments tested in this trial
- Not listed
Trial groups
No trial groups listed
Sponsors and collaborators
Source ClinicalTrials.gov