Gene Therapy for Subjects With RPGR Mutation-associated X-linked Retinitis Pigmentosa

Trial statusRecruiting
Trial phaseEarly Phase 1
Trial typeInterventional
Biological sexMale
Age8-45
SponsorFrontera Therapeutics

About this trial

A clinical trial of gene therapy for patients with X-linked retinitis pigmentosa (XLRP).

Eligibility criteria

Qualifiers

None

Disqualifiers

None

Trial design

Treatments tested in this trial

  • FT-002

Treatment groups

18 Participants
are divided into 3 treatment groups

Sponsors and collaborators

Frontera Therapeutics

Lead sponsor

Eye & ENT Hospital of Fudan University

Collaborator

Peking Union Medical College Hospital

Collaborator

Henan Provincial People's Hospital

Collaborator