Natural History of SMA
ConditionMuscular Atrophy, Spinal
Trial statusRecruiting
Trial phaseNot listed
Trial typeObservational
Biological sexAll
AgeNot listed
SponsorFondazione Policlinico Universitario Agostino Gemelli IRCCS
This is an investigator initiated observational study with the aim to record several aspects of function, care and adverse events in a large cohort of SMA patients followed longitudinally by using a structured academic disease registry.
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Fondazione Policlinico Universitario Agostino Gemelli IRCCS
Lead sponsor
University of Milan
Collaborator
Istituto Giannina Gaslini
Collaborator
Ospedale Pediatrico Bambin Gesù
Collaborator
University of Messina
Collaborator