Olutasidenib for the Treatment of Patients With IDH1 Mutated AML, MDS or CMML After Donor Hematopoietic Cell Transplant

Trial statusRecruiting
Trial phasePhase 1
Trial typeInterventional
Biological sexAll
Age18+
SponsorCity of Hope Medical Center

About this trial

This phase I trial tests the safety, side effects, and effectiveness of olutasidenib in preventing the return of disease (relapse) in patients who have undergone donor (allogeneic) hematopoietic cell transplant for acute myeloid leukemia (AML), myelodysplastic syndrome (MDS), or chronic myelomonocytic leukemia (CMML) carrying an IDH1 mutation. Olutasidenib is in a class of medications called IDH1 inhibitors. It works by slowing or stopping the growth of cancer cells. Giving olutasidenib may be safe, tolerable and/or effective in preventing relapse in patients with IDH1 mutated AML, MDS or CMML after an allogeneic hematopoietic cell transplant.

Eligibility criteria

This trial does not accept healthy volunteers

Qualifiers

Documented informed consent of the participant and/or legally authorized representative

Agreement to allow the use of archival tissue from diagnostic tumor biopsies. If unavailable, exceptions may be granted with study principal investigator (PI) approval

Age: ≥ 18 years

Eastern Cooperative Oncology Group (ECOG) ≤ 2 or Karnofsky performance status (KPS) ≥ 70

Disqualifiers

Patients with more than one allogeneic HCT

History of allergic reactions attributed to compounds of similar chemical or biological composition to study agent

Active diarrhea considered clinically significant and may impair oral drug administration

Clinically significant uncontrolled illness

Trial design

Design model

Single group

Treatments tested in this trial

  • Biospecimen Collection

    Procedure/Surgery

    Undergo blood sample collection

  • Olutasidenib

    Drug

    Given PO

Treatment groups

15 Participants
are divided into 1 treatment group
Group A: Treatment (olutasidenib)Experimental treatment 2 interventions

Trial outcomes

Primary outcomes

1

Incidence of adverse events (AEs)

AEs will be graded according to National Cancer Institute Common Terminology Criteria for Adverse Events version 5.0.

Time frame
Up to 30 days after last dose of study treatment
2

Proportion of patients completing at least 6 months of study therapy

Tolerability will be defined as the proportion of patients who complete at least 6 months of study therapy.

Time frame
Up to 2 years

Secondary outcomes

1

Overall survival (OS)

OS will be analyzed using the Kaplan-Meier method.

Time frame
From start of treatment to death, assessed up to 2 years
2

Leukemia-free survival (LFS)

LFS will be analyzed using the Kaplan-Meier method.

Time frame
From start of treatment to relapse or death, assessed up to 2 years
3

Time to relapse

Time to relapse will be analyzed using the curves of cumulative incidence.

Time frame
From start of treatment to relapse, assessed up to 2 years
4

Non-relapse mortality (NRM)

NRM will be analyzed using the curves of cumulative incidence.

Time frame
From start of treatment to death from causes other than relapse, assessed up to 2 years

Other outcomes

Sponsors and contacts

Click on the lead sponsor to view all of their trials.

City of Hope Medical Center

Lead sponsor

National Cancer Institute (NCI)

Collaborator