TAVNEOS for Otolaryngologic Manifestations of Granulomatosis With Polyangiitis

Trial statusNot yet recruiting
Trial phasePhase 2, Phase 3
Trial typeInterventional
Biological sexAll
Age18+
SponsorRobert Spiera, MD

About this trial

This is a single center double-blind placebo-controlled study. Patients with GPA and active ears, nose, and throat (ENT) disease in at least two ENT domains, as defined after endoscopic visualization of the upper airway and audiometric evaluation, if applicable, by a single otolaryngologist using a validated GPA ENT disease activity score, will be eligible for inclusion. Patients will be treated with standard of care (SOC) treatment as determined by their treating rheumatologist. In addition to SOC, patients will be randomized to receive TAVNEOS 30mg BID or placebo. Patients will be followed for 52 weeks with standardized ENT assessment along with rheumatologic evaluation of overall disease activity with BVAS.

Eligibility criteria

Qualifiers

GPA diagnosis defined by score of ≥5 on 2022 ACR/EULAR Classification Criteria for GPA

Bloody rhinorrhea (Daily blood stained nasal discharge)

Objective stridor (Stridor assessed by doctor)

Inflammation on nasal examination (Ulcers, granulation, friable mucosa on rigid nasal endoscopy. Excluding crusting)

Disqualifiers

Creatinine >4.0mg/dl or GFR <15 at baseline or dependence on dialysis

Respiratory failure requiring mechanical ventilatory support or had experienced alveolar hemorrhage requiring invasive pulmonary ventilation support anticipated to last beyond the screening period of the study

Previous treatment with TAVNEOS within 6 months of screening

Inability to comply with study and/or follow-up procedures at investigator discretion.

Trial design

Treatments tested in this trial

  • Avacopan
  • Placebo

Treatment groups

30 Participants
are divided into 2 treatment groups

Sponsors and collaborators

Robert Spiera, MD

Lead sponsor

Hospital for Special Surgery, New York

Sponsor institution

Amgen

Collaborator