phenotypeS in Non Ambulant Duchenne Muscular Dystrophy
Trial statusRecruiting
Trial phaseNot listed
Trial typeObservational
Biological sexMale
Age8-35
SponsorFondazione Policlinico Universitario Agostino Gemelli IRCCS
About this trial
The aims of the study are to prospectively collect information on several aspects of function in non-ambulant DMD patients by using a structured battery of tests including motor, respiratory and cardiac function
Eligibility criteria
Qualifiers
Children with genetically confirmed diagnosis of Duchenne Muscular Dystrophy will be included in the study. We will include all Duchenne Muscular Dystrophy boys who have lost the ability to walk independently.
All patients in whom consent can be obtained will be enrolled with no
Disqualifiers
Patients lacking genetic confirmation of Duchenne Muscular Dystrophy
Patients still able to walk for more than 10 meters.
Trial design
Treatments tested in this trial
- Different Phenotypes of non ambulant patients with Duchenne Muscular Dystrophy
Treatment groups
No treatment groups listed
Sponsors and collaborators
Source ClinicalTrials.gov