Status: Recruiting
ADAPT Study: Long-term Safety Study of INZ-701 in Patients With ENPP1 Deficiency and ABCC6 Deficiency
The purpose of this study (Study INZ701-304 \[ADAPT\]) is to assess the long-term safety of INZ-701 in patients with ENPP1 Deficiency or ABCC6 Deficiency who have received INZ-701 in an existing clinical study and choose to continue dosing for the potential treatment of their condition.
Participants needed: 200
Trial details
Phase: Phase 2Age: 1+Biological sex: AllType: InterventionalSponsor: Inozyme PharmaUpdated: Nov 29, 2024Locations: 5
Eligibility criteria
Provide written or electronic informed consent after the nature of the study has... [+6]
In the opinion of the Investigator, presence of any clinically significant disea... [+4]