Health Trials

Biallelic RPE65 Mutation-associated Retinal Dystrophy

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Review clinical trials related to Biallelic RPE65 Mutation-associated Retinal Dystrophy. Use filters to narrow results by trial status, phase, treatment, biological sex and sponsor.

Condition / disease
Location
Status: Recruiting

Gene Therapy in Subjects With Biallelic RPE65 Mutation-associated Retinal Dystrophy

The goal of this clinical trial is to evaluate the safety, tolerability and efficacy of subretinal administration of FT-001 in subjects with biallelic RPE65 mutation-associated retinal dystrophy.

Participants needed: 9
Trial details
Phase: Phase 1, Phase 2Age: 8-45Biological sex: AllType: InterventionalSponsor: Frontera TherapeuticsUpdated: May 15, 2023Locations: 1
Eligibility criteria

Subjects who are able to understand and sign the ICF [+2]

Other interfering eye diseases [+6]

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