Bone Marrow Failure Disorders

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Review clinical trials related to Bone Marrow Failure Disorders. Use filters to narrow results by trial status, phase, treatment, biological sex and sponsor.

Condition / disease
Location
Status: Not yet recruiting

Prenatal Transplantation for Fetuses With Fanconi Anemia

The investigators aim to evaluate the safety and efficacy of in utero hematopoietic stem cell transplantation (IUHSCT) for the treatment of fetuses diagnosed with Fanconi anemia (FA) during pregnancy.

Participants needed: 12
Trial details
Phase: Phase 1, Phase 2Biological sex: AllType: InterventionalSponsor: Agnieszka CzechowiczUpdated: Jun 16, 2026Locations: 2
Eligibility criteria

Male or female fetuses from 19^0/7 - 28^0/7 weeks gestational age at time of tra... [+3]

Fetal Participant Exclusion Criteria: Major anatomic or genetic anomalies that c... [+1]