Health Trials

Charcot-Marie-Tooth Disease Type 4J

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Review clinical trials related to Charcot-Marie-Tooth Disease Type 4J. Use filters to narrow results by trial status, phase, treatment, biological sex and sponsor.

Condition / disease
Location
Status: Not yet recruiting

Study of Intrathecal ELP-02 for Charcot-Marie-Tooth Disease Type 4J (CMT4J)

First-in-human Phase 1/2, open-label study to evaluate the safety, tolerability, and efficacy of a single lumbar intrathecal dose of ELP-02 to individuals with CMT4J.

Participants needed: 8
Trial details
Phase: Phase 1, Phase 2Age: 3-20Biological sex: AllType: InterventionalSponsor: Elpida Therapeutics SPCUpdated: Mar 3, 2026
Eligibility criteria

Male and females between the ages of 3 and 20 years at the time of screening. [+7]

Prior or ongoing medical condition, medical history, physical findings, cardiova... [+16]

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