Status: Recruiting
The ENERGY Study: Evaluation of Safety and Tolerability of INZ-701 in Infants With ENPP1 Deficiency or ABCC6 Deficiency
The primary purpose of Study INZ701-104 (the ENERGY study) is to assess the safety and tolerability of INZ-701 in infants with ENPP1 Deficiency or with ABCC6 Deficiency.
Participants needed: 16
Trial details
Phase: Phase 1Age: Up to 1Biological sex: AllType: InterventionalSponsor: Inozyme PharmaUpdated: Mar 24, 2026Locations: 7
Eligibility criteria
Infant aged ≤ 1 year at the time of enrollment [+4]
In the opinion of the Investigator, presence of any clinically significant disea... [+4]