Hereditary Transthyretin-mediated (hATTR) Amyloidosis

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Review clinical trials related to Hereditary Transthyretin-mediated (hATTR) Amyloidosis. Use filters to narrow results by trial status, phase, treatment, biological sex and sponsor.

Condition / disease
Location
Status: Recruiting

Patisiran-Lipid Nanoparticle (LNP) Pregnancy Surveillance Program

The purpose of this study is to collect and evaluate pregnancy outcomes, pregnancy complications, and fetal/neonatal/infant outcomes in women exposed to patisiran-LNP.

Participants needed: 10
Trial details
Biological sex: FemaleType: ObservationalSponsor: Alnylam PharmaceuticalsUpdated: Jun 1, 2026Locations: 7
Eligibility criteria

Documentation that the patient was exposed to patisiran-LNP at any point startin...

There are no exclusion criteria for participation in this program.