Status: Recruiting
A Study of Emapalumab for Pediatric Aplastic Anemia
The purpose of this study is to find out whether upfront emapalumab treatment can help in sAA (Aplastic Anemia) treatment planning and increase the effectiveness of standard treatment options. Funding Source- FDA OOPD
Participants needed: 35
Trial details
Phase: Phase 2Age: 0-25Biological sex: AllType: InterventionalSponsor: Memorial Sloan Kettering Cancer CenterUpdated: Dec 17, 2025Locations: 6
Eligibility criteria
Patients with severe cytopenias and a hypocellular marrow concerning for sAA [+3]
Uncontrolled infection at presentation. [+5]