Health Trials

Mucopolysaccharidosis Type II

1

Review clinical trials related to Mucopolysaccharidosis Type II. Use filters to narrow results by trial status, phase, treatment, biological sex and sponsor.

Condition / disease
Location
Status: Recruiting

A Multi-cohort Study of Safety, Efficacy, PK and PD of GNR-055 in Patients With Mucopolysaccharidosis Type II

This is phase 2/3 study to evaluate the safety, pharmacokinetics, pharmacodynamics, and efficacy of the investigational product GNR-055 in MPS II (Hunter syndrome) patients of different age groups.

Participants needed: 32
Trial details
Phase: Phase 2, Phase 3Biological sex: MaleType: InterventionalSponsor: AO GENERIUMUpdated: Jul 30, 2025Locations: 5
Eligibility criteria

Signed inform consent; [+4]

Clinically pronounced hypersensitivity to ID2S or any other component of the dru... [+3]

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