Organic Acidemias

1

Review clinical trials related to Organic Acidemias. Use filters to narrow results by trial status, phase, treatment, biological sex and sponsor.

Condition / disease
Location
Status: Recruiting

At Home Ammonia Monitoring of Inborn Errors of Ammonia Metabolism

The goal of this observational study is to learn if people with certain ammonia metabolism disorders will measure their ammonia levels at home. The main question it aims to answer is: • Will participants measure their ammonia every day? Participants will be asked to: * Attend two in-person study visits at the clinic. * Measure temperature, heart rate, and blood oxygen every day. * Complete a short survey every day. * Measure ammonia every day.

Participants needed: 30
Trial details
Age: 12+Biological sex: AllType: InterventionalSponsor: Sequitur Health Corp.Updated: May 27, 2026Locations: 1
Eligibility criteria

Confirmed ammonia disorder such as [+19]

Incarcerated [+2]