Health Trials

Retinal Dystrophy Due to Biallelic ABCA4 Mutations

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Review clinical trials related to Retinal Dystrophy Due to Biallelic ABCA4 Mutations. Use filters to narrow results by trial status, phase, treatment, biological sex and sponsor.

Condition / disease
Location
Status: Recruiting

Safety and Preliminary Efficacy of VG801 in Patients With ABCA4 Mutation-associated Retinal Dystrophy (Stargardt Disease)

This is a single-arm, open-label, non-randomized, single dose-escalation, first-in-human (FIH) clinical trial to evaluate the safety and preliminary efficacy of VG801 for treatment of patients with retinal dystrophy (Stargardt disease) due to biallelic ABCA4 mutations.

Participants needed: 15
Trial details
Phase: Phase 1, Phase 2Age: 6+Biological sex: AllType: InterventionalSponsor: VeonGen Therapeutics GmbHUpdated: Dec 11, 2025Locations: 1
Eligibility criteria

Written informed consent. [+4]

Pre-existing eye conditions such as uveitis, glaucoma, or diabetic retinopathy o... [+5]

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