Thymine Kinase 2 Deficiency

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Review clinical trials related to Thymine Kinase 2 Deficiency. Use filters to narrow results by trial status, phase, treatment, biological sex and sponsor.

Condition / disease
Location
Status: Available

Doxecitine and Doxribtimine-Expanded Access

This Expanded Access Record for doxecitine and doxribtimine includes the following managed access programs and status: * TK0113: Available * TK0115: No longer Available

Trial details
Biological sex: AllType: Expanded AccessSponsor: UCB BIOSCIENCES, Inc.Updated: Jun 5, 2026
Eligibility criteria

Pediatric and adult patients with a diagnosis of TK2d based on confirmed reporta... [+9]

Confirmed diagnosis of other genetic or polygenic disease likely to confound cli... [+20]