Status: Available
Expanded Access Program of Bitopertin For Participants With EPP or XLP
The goal of this expanded access program is to provide bitopertin to patients with EPP and XLP who have no satisfactory treatment options available in the US and to learn if bitopertin is safe to treat EPP and XLP.
Trial details
Age: 12+Biological sex: AllType: Expanded AccessSponsor: Disc Medicine, IncUpdated: Jun 30, 2026Locations: 3
Eligibility criteria
Written informed consent (and assent where applicable). [+4]
Known hypersensitivity to bitopertin or its excipients. [+13]