Health Trials

Clinical trials

2

Search and review clinical trials. Use filters to narrow results by trial status, phase, treatment, biological sex and sponsor.

Condition / disease
Location
Status: Available

Tideglusib: Expanded Access Use in Congenital Myotonic Dystrophy

This treatment plan is limited to a single patient with Congenital Myotonic Dystrophy, who is ineligible or otherwise unable to participate in ongoing clinical trials.

Trial details
Type: Expanded AccessSponsor: AMO Pharma LimitedUpdated: Aug 13, 2025
Eligibility criteria

Not listed

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Status: Recruiting

Safety and Efficacy of Tideglusib in Congenital or Childhood Onset Myotonic Dystrophy

This is an open-label phase 2/3 study for individuals with Congenital Myotonic Dystrophy (Congenital DM1) who participated in the preceding AMO-02-MD-2-003 study or individuals with either Congenital or Childhood Onset DM1 who are treatment naïve.

Participants needed: 76
Trial details
Phase: Phase 2, Phase 3Age: 6-45Biological sex: AllType: InterventionalSponsor: AMO Pharma LimitedUpdated: May 28, 2025Locations: 14
Eligibility criteria

Subjects under study must be individuals with a diagnosis of Congenital or Child... [+10]

Body mass index (BMI) less than 13.5 kg/m² or greater than 40 kg/m² [+6]

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