Health Trials

Clinical trials

2

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Condition / disease
Location
Status: Not yet recruiting

A Phase 3 Study of Fenfluramine Hydrochloride in Rett Syndrome

The purpose of this study is to investigate the efficacy of fenfluramine hydrochloride (HCl) versus placebo in study participants with Rett syndrome (RTT).

Participants needed: 200
Trial details
Phase: Phase 3Age: 5-35Biological sex: AllType: InterventionalSponsor: UCB BIOSCIENCES, Inc.Updated: Jun 26, 2026Locations: 9
Eligibility criteria

Participant has typical or classic Rett Syndrome (RTT) according to the RettSear... [+10]

Participant has a history of lymphoma, leukemia, or any malignancy within the pa... [+8]

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Status: Available

Doxecitine and Doxribtimine-Expanded Access

This Expanded Access Record for doxecitine and doxribtimine includes the following managed access programs and status: * TK0113: Available * TK0115: No longer Available

Trial details
Biological sex: AllType: Expanded AccessSponsor: UCB BIOSCIENCES, Inc.Updated: Jun 5, 2026
Eligibility criteria

Pediatric and adult patients with a diagnosis of TK2d based on confirmed reporta... [+9]

Confirmed diagnosis of other genetic or polygenic disease likely to confound cli... [+20]

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